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Enzyme replacement therapy is available. A bone marrow transplant may be needed in severe cases.
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The treatment team may vary, depending on the patient's specific symptoms. Early in the diagnostic phase, a geneticist may be helpful. If neurological problems predominate, a neurologist will be necessary. A hematologist may be consulted to handle...
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Until the 1990s, only supportive therapy could be offered. Analgesics are used to control pain. Orthopedic treatment is used for bone fractures . In some cases, surgical removal of the spleen may be necessary. Several treatments for anemia have be...
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The bone marrow—the sponge-like tissue found in the center of certain bones—contains stem cells that are the precursors of white blood cells, red blood cells, and platelets. These blood cells are vital for normal body functions, such as oxygen tra...
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A bone marrow transplant delivers healthy bone marrow stem cells into the patient. It replaces bone marrow that is either not working properly or has been destroyed (ablated) by chemotherapy or radiation.
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The bone marrow—the sponge-like tissue found in the center of certain bones—contains stem cells that are the precursors of white blood cells, red blood cells, and platelets. These blood cells are vital for normal body functions, such as oxygen tra...
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The bone marrow—the sponge-like tissue found in the center of certain bones—contains stem cells that are the precursors of white blood cells, red blood cells, and platelets. These blood cells are vital for normal body functions, such as oxygen tra...
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